Mean SD (min-max) | ||
---|---|---|
Age/years | 9.8 ± 5.6 (2–18) | |
Weight (in kg) | 38.1 ± 23 (8–80) | |
Height (in cm) | 124.2 ± 37.4 (60–178) | |
BSA | 1.12 ± 0.51 (0.42–1.98) | |
Sex | N | % |
Male | 18 | 40.9 |
Female | 26 | 59.1 |
Family history | 5 | 11.4 |
Consanguinity | 5 | 11.4 |
Major adverse effects* | 14 | 31.8 |